GRAND RAPID, Mich. — At just 26 months old, Grace Visser was diagnosed with Rett Syndrome, a rare genetic disorder that affects brain development. Grace and her family have faced a journey ...

Sophomore Grace Rett was the only person who died in the crash early Wednesday morning Joelle Goldstein is a Senior News Editor on the TV team for PEOPLE Digital. She has been with the brand since ...

but the reach of Giggles & Grace goes beyond just one disease. The nonprofit serves families dealing with over 15 rare diseases, including Ehlers-Danlos Syndrome and Rett Syndrome, both of which ...

The patient affected by a serious adverse event in Neurogene's clinical trial of Rett syndrome gene therapy has now died, but that won't cause the study to be halted. The FDA has allowed the ...

Denali Therapeutics, Neurogene, Larimar Therapeutics, and Grace Science will be the first ... Neurogene has contributed its gene therapy NGN-401 for Rett syndrome, a rare genetic neurological ...

Phase 2a TREE study assesses safety and efficacy of leriglitazone Minoryx Therapeutics has dosed the first patient in its phase 2a TREE study, which evaluates the safety and efficacy of leriglitazone ...

The Blue Bird Circle Rett Center at Baylor College of Medicine is composed of a multidisciplinary team of health professionals. Several BCM physicians are involved clinically at the Blue Bird Circle ...

TRUMBULL, Conn., March 13, 2025 (GLOBE NEWSWIRE) -- The Rett Syndrome Research Trust (RSRT), the organization working to cure Rett syndrome, is pleased to announce that Amy Gilliland, President of ...

(RTTNews) - Acadia Pharmaceuticals Inc. (ACAD) announced the publication of clinical data from the open-label DAFFODIL study, which evaluated the long-term safety and efficacy of DAYBUE or ...