Taysha Gene Therapies offers hope for Rett syndrome with innovative treatment, strong trial results, and promising regulatory ...

Rett syndrome is a neurodevelopmental disorder that primarily affects girls, most of whom have mutations in the transcription regulatory gene MECP2. However, mutations in MECP2 also have been ...

If granted marketing authorization, trofinetide will be the first and only approved therapy for Rett syndrome in the European Union (EU). Trofinetide is already approved in the United States and ...

Trofinetide is intended to treat Rett syndrome, a neurodevelopmental disorder. Credit: SewCreamStudio/Shutterstock. Acadia Pharmaceuticals has submitted a marketing ...

The news: Neuren Pharmaceuticals' Rett syndrome treatment, trofinetide, is a step closer to receiving regulatory approval in the European Union, after its US partner Acadia Pharmaceuticals submitted a ...

Neuren’s partner Acadia Pharmaceuticals submits marketing authorisation application in Europe for trofinetide for treatment of Rett syndrome Compumedics achieves a record $32.8m in sales orders in H1 ...

How big of a problem is it worldwide? By The Learning Network A new collection of graphs, maps and charts organized by topic and type from our “What’s Going On in This Graph?” feature.

If you haven't heard of Rett syndrome, it's probably because it's very rare. Affecting an estimated one in 12,000 baby girls born each year (and only rarely seen in boys), this genetic disorder ...

asked European regulators to approve Neuren's treatment for the rare genetic disorder known as Rett syndrome. The Australian dollar was near a one-week high against the greenback, buying 62.02 US ...

Linear equations can be shown on a graph. Find out how to create one in this Bitesize KS3 maths video. A quadratic function can be drawn as a parabola on a graph. Find out how to plot the graph in ...