Study harnesses a cell-type-specific, multi-target drug discovery strategy grounded in human data and real-world evidence.

An antibody treatment successfully prepared patients for stem cell transplants without toxic chemotherapy or radiation.

VISTA, an AI-controlled data loop system, guides large-scale antibody design from scratch for applications in cancer therapy.

Sarepta Therapeutics said it will voluntarily “and temporarily” pause all shipments of Elevidys® (delandistrogene ...

Using data from the T2T reference, scientists linked two new genes to changes in brain size and synapse signaling.

Highlights of the Sanner facility include a 60,500-sq-ft site equipped with GMP-certified cleanrooms (ISO class 7 & 8) and ...

Prime editing corrects the most common genetic mutations that cause alternating hemiplegia of childhood (AHC), a rare and severe neurological disorder.