FDA assigns Prescription Drug User Fee Act (PDUFA) target date of December 10, 2025 Ayrmid Ltd. (“Ayrmid” or the “Company”), the parent company of Gamida Cell Inc., a cell therapy pioneer working to ...

A Prescription Drug User Fee Act target date of December 10, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the supplemental Biologics ...

Eltrombopag combined with immunosuppressive therapy in pediatric patients with severe aplastic anemia achieved a 54.9% overall response rate at 26 weeks, with a 71.4% response in relapsed/refractory ...

Anemia affects almost 1 in 4 people worldwide. But while billions of people live with the disease, its signs and symptoms aren’t just part of everyday life. “Anemia is one of the most common global ...

FRAMINGHAM – The Worlds passed him by. Then sectionals. And next month, states will as well. Joshua Peace is back throwing this spring with a focus on recapturing not what he lost – senior year ...

A groundbreaking new study introduces an AI-powered smartphone app that noninvasively screens for anemia using a photo of a user's fingernail. The study shows the app provides hemoglobin estimates ...

Mutations in FANCX appear to cause a lethal form of Fanconi anemia, a finding that sheds light on unexplained pregnancy loss and offers new avenues for genetic screening. Fanconi anemia is an ...

Tia Szczepanski, 29, is a pediatric nurse in the ICU at Albany Medical Center and has not been able to go to work recently. That’s because she has been diagnosed with severe aplastic anemia and now ...

ALBANY, N.Y. — The Capital Region is coming together to support Tia Szcepanski, a dedicated pediatric nurse at Albany Medical Center and a traveling nurse to Syracuse, who has been diagnosed with ...

NORTH CHARLESTON, S.C. (WCSC) - A six-year-old diagnosed with a rare disease is sharing his experience in hopes that other kids like him will never have to feel alone. Jaxson “Jax” Foxwell is similar ...

Please provide your email address to receive an email when new articles are posted on . Prior trials established the role of haploidentical BMT for severe aplastic anemia. Two trials underway have the ...

A patient on Long Island is the first in New York to be cured of sickle cell anemia, doctors say. They credit state-of-the-art genetic treatment. Medical history made at Cohen Children's Medical ...